Lifetime Achievement Award
Abbey S. Meyers Leadership Award
Rare Impact Award
Rare Impact Award
Rare Impact Award
Rare Impact Award
Rare Impact Award
bluebird bio for Skysona®
CSL Behring and uniQure for Hemgenix®
Mallinckrodt Pharmaceuticals for Terlivaz®
Marinus Pharmaceuticals for Ztalmy®
Novartis for Vijoice®
Sanofi for Xenpozyme™